Δευτέρα 8 Μαΐου 2017

Allele-Selective Suppression of Mutant Huntingtin in Primary Human Blood Cells

Miller, JRC; Pfister, EL; Liu, W; Andre, R; Träger, U; Kennington, LA; Lo, K; Miller, JRC; Pfister, EL; Liu, W; Andre, R; Träger, U; Kennington, LA; Lo, K; Dijkstra, S; Macdonald, D; Ostroff, G; Aronin, N; Tabrizi, SJ; - view fewer (2017) Allele-Selective Suppression of Mutant Huntingtin in Primary Human Blood Cells. Scientific Reports , 7 , Article 46740. 10.1038/srep46740 . Green open access

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