The utility of the FIPI score in predicting long-term clinical outcomes in patients with Fabry disease receiving enzyme replacement therapy with agalsidase alfa

Mac Lochlainn, DJ; McKechnie, DGJ; Mehta, AB; Hughes, DA; (2018) The utility of the FIPI score in predicting long-term clinical outcomes in patients with Fabry disease receiving enzyme replacement therapy with agalsidase alfa. Molecular Genetics and Metabolism , 123 (2) pp. 154-158. 10.1016/j.ymgme.2017.10.001 .

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