Impact of long-term elosulfase alfa on activities of daily living in patients with Morquio A syndrome in an open-label, multi-center, phase 3 extension study

Hendriksz, CJ; Parini, R; AlSayed, MD; Raiman, J; Giugliani, R; Mitchell, JJ; Burton, BK; ... Harmatz, PR; + view all Hendriksz, CJ; Parini, R; AlSayed, MD; Raiman, J; Giugliani, R; Mitchell, JJ; Burton, BK; Guelbert, N; Stewart, FJ; Hughes, DA; Matousek, R; Hawley, SM; Decker, C; Harmatz, PR; - view fewer (2018) Impact of long-term elosulfase alfa on activities of daily living in patients with Morquio A syndrome in an open-label, multi-center, phase 3 extension study. Molecular Genetics and Metabolism , 123 (2) pp. 127-134. 10.1016/j.ymgme.2017.11.015 . Green open access

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