A novel adeno-associated virus capsid with enhanced neurotropism corrects a lysosomal transmembrane enzyme deficiency.

Tordo, J; O'Leary, C; Antunes, ASLM; Palomar, N; Aldrin-Kirk, P; Basche, M; Bennett, A; ... Henckaerts, E; + view all Tordo, J; O'Leary, C; Antunes, ASLM; Palomar, N; Aldrin-Kirk, P; Basche, M; Bennett, A; D'Souza, Z; Gleitz, H; Godwin, A; Holley, RJ; Parker, H; Liao, AY; Rouse, P; Youshani, AS; Dridi, L; Martins, C; Levade, T; Stacey, KB; Davis, DM; Dyer, A; Clément, N; Björklund, T; Ali, RR; Agbandje-McKenna, M; Rahim, AA; Pshezhetsky, A; Waddington, SN; Linden, RM; Bigger, BW; Henckaerts, E; - view fewer (2018) A novel adeno-associated virus capsid with enhanced neurotropism corrects a lysosomal transmembrane enzyme deficiency. Brain 10.1093/brain/awy126 . (In press). Green open access

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