Treatment of Fabry’s Disease with the Pharmacologic Chaperone Migalastat

Germain, DP; Hughes, DA; Nicholls, K; Bichet, DG; Giugliani, R; Wilcox, WR; Feliciani, C; Germain, DP; Hughes, DA; Nicholls, K; Bichet, DG; Giugliani, R; Wilcox, WR; Feliciani, C; Shankar, SP; Ezgu, F; Amartino, H; Bratkovic, D; Feldt-Rasmussen, U; Nedd, K; Sharaf El Din, U; Lourenco, CM; Banikazemi, M; Charrow, J; Dasouki, M; Finegold, D; Giraldo, P; Goker-Alpan, O; Longo, N; Scott, CR; Torra, R; Tuffaha, A; Jovanovic, A; Waldek, S; Packman, S; Ludington, E; Viereck, C; Kirk, J; Yu, J; Benjamin, ER; Johnson, F; Lockhart, DJ; Skuban, N; Castelli, J; Barth, J; Barlow, C; Schiffmann, R; - view fewer (2016) Treatment of Fabry's Disease with the Pharmacologic Chaperone Migalastat. New England Journal of Medicine , 375 (6) pp. 545-555. 10.1056/NEJMoa1510198 . Green open access

http://ift.tt/2q7uFBw